| # | % | |||||
|---|---|---|---|---|---|---|
| 1 | WAVE LIFE SCIENCES LTD | 7,088,651 | 146,664,000 | 20.31% | ||
| 2 | ACHILLION PHARMACEUTICALS INC COM | 12,033,220 | 93,859,000 | 13.00% | ||
| 3 | AXOVANT SCIENCES LTD | 5,000,000 | 64,200,000 | 8.89% | ||
| 4 | AVEXIS INC COM | 1,339,382 | 50,923,000 | 7.05% | ||
| 5 | ACLARIS THERAPEUTICS INC COM | 2,627,719 | 48,534,000 | 6.72% | ||
| 6 | NEKTAR THERAPEUTICS COM | 3,224,854 | 45,890,000 | 6.35% | ||
| 7 | Ascendis Pharma | 3,412,857 | 45,289,000 | 6.27% | ||
| 8 | TG THERAPEUTICS INC COM | 4,531,714 | 27,462,000 | 3.80% | ||
| 9 | ARDELYX INC COM | 2,312,243 | 20,186,000 | 2.79% | ||
| 10 | ZOGENIX INC | 2,451,237 | 19,732,000 | 2.73% | ||
| 11 | VITAE PHARMACEUTICALS INC | 1,575,000 | 16,994,000 | 2.35% | ||
| 12 | AIMMUNE THERAPEUTICS INC COM | 1,292,940 | 13,990,000 | 1.94% | ||
| 13 | ALCOBRA LTD | 3,032,911 | 13,618,000 | 1.89% | ||
| 14 | Proteon Therapeutics | 1,626,931 | 13,064,000 | 1.81% | ||
| 15 | Aquinox Pharmaceuticals Inc | 1,691,977 | 11,201,000 | 1.55% | ||
| 16 | Strongbridge Biopharma plc | 2,675,338 | 10,648,000 | 1.47% | ||
| 17 | NATERA INC | 783,520 | 9,453,000 | 1.31% | ||
| 18 | DIMENSION THERAPEUTICS INC COM | 1,548,033 | 9,288,000 | 1.29% | ||
| 19 | BIOCRYST PHARMACEUTICALS | 2,989,795 | 8,491,000 | 1.18% | ||
| 20 | Dicerna Pharmaceuticals | 2,428,571 | 7,286,000 | 1.01% | ||
| 21 | SANGAMO BIOSCIENCES INCORPORATED | 1,165,938 | 6,751,000 | 0.93% | ||
| 22 | Agile Therapeutics, Inc. | 853,151 | 6,492,000 | 0.90% | ||
| 23 | TENAX THERAPEUTICS INC COM | 2,389,700 | 6,118,000 | 0.85% | ||
| 24 | EIGER BIOPHARMACEUTICALS INC | 291,700 | 5,781,000 | 0.80% | ||
| 25 | BEIGENE LTD | 170,000 | 5,066,000 | 0.70% | ||
| 26 | CIDARA THERAPEUTICS INC | 410,809 | 4,235,000 | 0.59% | ||
| 27 | AKARI THERAPEUTICS PLC | 234,240 | 3,160,000 | 0.44% | ||
| 28 | AEGLEA BIOTHERAPEUTICS INC COM | 521,550 | 2,535,000 | 0.35% | ||
| 29 | MERUS N V | 237,599 | 1,898,000 | 0.26% | ||
| 30 | ZYNERBA PHARMACEUTICALS INC | 253,468 | 1,736,000 | 0.24% | ||
| 31 | ARCA BIOPHARMA INCORPORATED COM PAR .001 | 562,693 | 1,632,000 | 0.23% | ||
| 32 | ProNAi Therapeutics, Inc. | 29,719 | 59,000 | 0.01% |
Portfolio data is normalized using SEC Form 13F filings, including the Original 13F-HR (0001144204-16-119492, filed 2016.08.15).
From 2023-01-03 onward, the SEC requires values to be reported in nearest dollars. Earlier filings reported values in thousands; therefore, positions shown as $0 in older filings may represent actual values between $0–$999.