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Institutional Investment Manager
RA CAPITAL MANAGEMENT, L.P.
RA CAPITAL MANAGEMENT, L.P. (CIK: 0001346824) incorporated in Delaware, located at 200 Berkeley Street, 18th Floor, Boston, MA. Institutional holdings reported to the SEC.

Institutional Holdings (2015Q2)
Portfolio Summary: 59 holdings with a total value of $994,105,000.
#
Name
Shares
Value ($)
%
Options
Notes
1 AXOVANT SCIENCES LTD 5,000,000 101,900,000 10.25%
2 ACHILLION PHARMACEUTICALS INC COM 9,945,997 88,122,000 8.86%
3 DYAX CORP COM CVR 2,703,093 71,632,000 7.21%
4 SANGAMO BIOSCIENCES INCORPORATED 6,000,000 66,540,000 6.69% Call
5 TG THERAPEUTICS INC COM 3,302,213 54,784,000 5.51%
6 REGULUS THERAPEUTICS INC 3,790,476 41,544,000 4.18%
7 COHERUS BIOSCIENCES INC COM 1,380,320 39,891,000 4.01%
8 BIOCRYST PHARMACEUTICALS 2,605,361 38,898,000 3.91%
9 Dicerna Pharmaceuticals 2,428,571 33,879,000 3.41%
10 Ascendis Pharma 1,913,153 33,825,000 3.40%
11 COLLEGIUM PHARMACEUTICAL INC COM 1,545,410 27,570,000 2.77%
12 ARDELYX INC COM 1,719,945 27,468,000 2.76%
13 Proteon Therapeutics 1,506,872 26,913,000 2.71%
14 XENCOR INC COM 1,075,410 23,627,000 2.38%
15 BLUEPRINT MEDICINES CORP COM 878,348 23,267,000 2.34%
16 BELLICUM PHARMACEUTICALS INC COM 1,026,402 21,832,000 2.20%
17 MEDICINES CO 705,925 20,197,000 2.03%
18 BLUEBIRD BIO INCORPORATED 109,383 18,417,000 1.85%
19 DYNAVAX TECHNOLOGIES CORP 766,000 17,944,000 1.81%
20 CIDARA THERAPEUTICS INC 1,141,333 16,001,000 1.61%
21 NOVAVAX INC COM 1,431,232 15,944,000 1.60%
22 JUNO THERAPEUTICS INCORPORATED 280,000 14,932,000 1.50%
23 AGENUS INC 1,600,000 13,808,000 1.39%
24 SANGAMO BIOSCIENCES INCORPORATED 1,220,209 13,532,000 1.36%
25 OMEROS CORP 749,000 13,475,000 1.36%
26 THERAPEUTICSMD INC 1,680,395 13,208,000 1.33%
27 Agile Therapeutics, Inc. 1,458,792 12,531,000 1.26%
28 Nivalis Therapeutics Inc 757,263 11,473,000 1.15%
29 SERES THERAPEUTICS INC 246,645 10,236,000 1.03%
30 ALCOBRA LTD 1,525,894 9,979,000 1.00%
31 CONCERT PHARMACEUTICALS INC COM 668,406 9,953,000 1.00%
32 TENAX THERAPEUTICS INC COM 2,670,300 9,853,000 0.99%
33 SUCAMPO PHARMACEUTICALS INC 450,000 7,394,000 0.74%
34 ARCA BIOPHARMA INC COM NEW 5,678,592 6,530,000 0.66%
35 AURIS MED HLDG AG 940,000 4,568,000 0.46%
36 AURINIA PHARMACEUTICALS INC 1,142,676 3,451,000 0.35%
37 TREVENA INC 528,118 3,306,000 0.33%
38 T2 BIOSYSTEMS INC 138,002 2,240,000 0.23%
39 Vical Inc 2,606,978 1,825,000 0.18%
40 BIOTA PHARMACEUTIALS INC COM 807,855 1,672,000 0.17%
41 SANOFI SPOND FUNSPONSORED ADR 116,400 1,439,000 0.14%
42 TESARO INC 23,500 1,382,000 0.14%
43 NEWLINK GENETICS CORP 30,000 1,328,000 0.13%
44 REGENERON PHARMACEUTICALS 2,450 1,250,000 0.13%
45 PTC THERAPEUTICS INC 25,800 1,242,000 0.12%
46 ALKERMES PLC SHS 19,200 1,235,000 0.12%
47 NEUROCRINE BIOSCIE COM USD0.001 24,400 1,165,000 0.12%
48 CLOVIS ONCOLOGY INC 13,200 1,160,000 0.12%
49 ACADIA PHARMACEUTICALS INC COM 27,300 1,143,000 0.11%
50 INCYTE 10,700 1,115,000 0.11%
Page 1 of 2

Portfolio data is normalized using SEC Form 13F filings, including the Original 13F-HR (0001144204-15-049028, filed 2015.08.13).

From 2023-01-03 onward, the SEC requires values to be reported in nearest dollars. Earlier filings reported values in thousands; therefore, positions shown as $0 in older filings may represent actual values between $0–$999.