| # | % | |||||
|---|---|---|---|---|---|---|
| 1 | WAVE LIFE SCIENCES LTD | 7,088,651 | 230,168,000 | 23.74% | ||
| 2 | ACHILLION PHARMACEUTICALS INC COM | 12,033,220 | 97,469,000 | 10.05% | ||
| 3 | Ascendis Pharma | 3,681,491 | 73,998,000 | 7.63% | ||
| 4 | AVEXIS INC COM | 1,732,274 | 71,387,000 | 7.36% | ||
| 5 | AXOVANT SCIENCES LTD | 5,000,000 | 70,000,000 | 7.22% | ||
| 6 | NEKTAR THERAPEUTICS COM | 3,664,154 | 62,950,000 | 6.49% | ||
| 7 | ARDELYX INC COM | 3,266,045 | 42,263,000 | 4.36% | ||
| 8 | ACLARIS THERAPEUTICS INC COM | 1,547,152 | 39,623,000 | 4.09% | ||
| 9 | TG THERAPEUTICS INC COM | 4,631,114 | 35,845,000 | 3.70% | ||
| 10 | ZOGENIX INC | 2,656,166 | 31,451,000 | 3.24% | ||
| 11 | Aquinox Pharmaceuticals Inc | 2,191,977 | 29,285,000 | 3.02% | ||
| 12 | AIMMUNE THERAPEUTICS INC COM | 1,292,940 | 19,394,000 | 2.00% | ||
| 13 | Foamix Pharmaceuticals Ltd. | 1,820,138 | 16,854,000 | 1.74% | ||
| 14 | Protagonist Therapeutics, Inc. | 754,411 | 15,941,000 | 1.64% | ||
| 15 | Proteon Therapeutics | 1,626,931 | 15,179,000 | 1.57% | ||
| 16 | Dicerna Pharmaceuticals | 2,428,571 | 14,280,000 | 1.47% | ||
| 17 | BIOCRYST PHARMACEUTICALS | 2,989,795 | 13,185,000 | 1.36% | ||
| 18 | Strongbridge Biopharma plc | 2,501,667 | 13,059,000 | 1.35% | ||
| 19 | Audentes Therapeutics, Inc. | 707,426 | 12,599,000 | 1.30% | ||
| 20 | DIMENSION THERAPEUTICS INC COM | 1,548,033 | 12,369,000 | 1.28% | ||
| 21 | ACCELERON PHARMA | 318,565 | 11,529,000 | 1.19% | ||
| 22 | ARROWHEAD PHARMACEUTICALS IN | 1,525,424 | 11,212,000 | 1.16% | ||
| 23 | TENAX THERAPEUTICS INC COM | 2,389,700 | 5,532,000 | 0.57% | ||
| 24 | BEIGENE LTD | 170,000 | 5,238,000 | 0.54% | ||
| 25 | ALCOBRA LTD | 2,044,756 | 5,051,000 | 0.52% | ||
| 26 | EIGER BIOPHARMACEUTICALS INC | 354,200 | 4,743,000 | 0.49% | ||
| 27 | SANGAMO BIOSCIENCES INCORPORATED | 899,438 | 4,164,000 | 0.43% | ||
| 28 | AEGLEA BIOTHERAPEUTICS INC COM | 336,134 | 2,155,000 | 0.22% | ||
| 29 | ARCA BIOPHARMA INCORPORATED COM PAR .001 | 521,606 | 1,476,000 | 0.15% | ||
| 30 | AKARI THERAPEUTICS PLC | 114,039 | 970,000 | 0.10% |
Portfolio data is normalized using SEC Form 13F filings, including the Original 13F-HR (0001144204-16-134325, filed 2016.11.14).
From 2023-01-03 onward, the SEC requires values to be reported in nearest dollars. Earlier filings reported values in thousands; therefore, positions shown as $0 in older filings may represent actual values between $0–$999.