| # | % | |||||
|---|---|---|---|---|---|---|
| 1 | WAVE LIFE SCIENCES LTD | 7,088,651 | 185,368,000 | 27.07% | ||
| 2 | Ascendis Pharma | 5,409,990 | 109,498,000 | 15.99% | ||
| 3 | AVEXIS INC COM | 1,890,796 | 90,248,000 | 13.18% | ||
| 4 | ACHILLION PHARMACEUTICALS INC COM | 13,633,220 | 56,305,000 | 8.22% | ||
| 5 | Aquinox Pharmaceuticals Inc | 2,191,977 | 36,190,000 | 5.29% | ||
| 6 | ZOGENIX INC | 2,451,237 | 29,783,000 | 4.35% | ||
| 7 | ARDELYX INC COM | 1,935,305 | 27,481,000 | 4.01% | ||
| 8 | Foamix Pharmaceuticals Ltd. | 1,820,138 | 20,204,000 | 2.95% | ||
| 9 | BIOCRYST PHARMACEUTICALS | 2,989,795 | 18,925,000 | 2.76% | ||
| 10 | RA PHARMACEUTICALS INC | 1,190,270 | 18,080,000 | 2.64% | ||
| 11 | Protagonist Therapeutics, Inc. | 692,563 | 14,634,000 | 2.14% | ||
| 12 | AIMMUNE THERAPEUTICS INC COM | 677,663 | 13,858,000 | 2.02% | ||
| 13 | Audentes Therapeutics, Inc. | 532,426 | 9,727,000 | 1.42% | ||
| 14 | BEIGENE LTD | 240,000 | 7,286,000 | 1.06% | ||
| 15 | Dicerna Pharmaceuticals | 2,428,571 | 6,994,000 | 1.02% | ||
| 16 | ABEONA THERAPEUTICS INC | 1,142,857 | 5,543,000 | 0.81% | ||
| 17 | Strongbridge Biopharma plc | 2,279,099 | 5,470,000 | 0.80% | ||
| 18 | TG THERAPEUTICS INC COM | 1,004,314 | 4,670,000 | 0.68% | ||
| 19 | TENAX THERAPEUTICS INC COM | 2,389,700 | 4,660,000 | 0.68% | ||
| 20 | KALVISTA PHARMACEUTICALS INC | 591,070 | 4,179,000 | 0.61% | ||
| 21 | EIGER BIOPHARMACEUTICALS INC | 354,200 | 4,126,000 | 0.60% | ||
| 22 | DIMENSION THERAPEUTICS INC COM | 928,199 | 4,038,000 | 0.59% | ||
| 23 | IDERA PHARMACEUTICALS INC | 2,250,000 | 3,375,000 | 0.49% | ||
| 24 | MEDICINES CO | 79,899 | 2,712,000 | 0.40% | ||
| 25 | AKARI THERAPEUTICS PLC | 101,439 | 714,000 | 0.10% | ||
| 26 | ARCA BIOPHARMA INCORPORATED COM PAR .001 | 232,245 | 662,000 | 0.10% |
Portfolio data is normalized using SEC Form 13F filings, including the Original 13F-HR (0001144204-17-008904, filed 2017.02.14).
From 2023-01-03 onward, the SEC requires values to be reported in nearest dollars. Earlier filings reported values in thousands; therefore, positions shown as $0 in older filings may represent actual values between $0–$999.